The state of Mississippi currently has 1 active clinical trials seeking participants for Hereditary Angioedema (HAE) research studies. These trials are conducted in various cities, including Jackson, Tupelo, Hattiesburg and Flowood.
A Gene Therapy Study of BMN 331 in Subjects With Hereditary Angioedema
Recruiting
This is a Phase 1/2, single-arm, open-label, dose-escalation and dose-expansion study of BMN 331 for the treatment of hereditary angioedema (HAE) due to C1 Esterase Inhibitor (C1-INH) protein deficiency. The study drug BMN 331is identified as AAV5 hSERPING1, an adeno-associated virus (AAV5)-based gene therapy vector that expresses wild-type human C1 Esterase Inhibitor (hC1-INH), under the control of a liver-selective promoter, and is being developed for the treatment of HAE with C1-INH deficienc... Read More
Gender:
All
Ages:
18 years and above
Trial Updated:
12/05/2023
Locations: Mississippi Center for Advanced Medicine, Madison, Mississippi
Conditions: Hereditary Angioedema, HAE